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01/08/2024
PHASE 2 EFFICACY AND SAFETY OF RILIPRUBART, A C1S-COMPLEMENT INHIBITOR, IN CHRONIC INFLAMMATORY DEMYELINATING POLYNEUROPATHY
Querol, L, Lewis, RA, Hartung, HP, Van Doorn, PA, Wallstroem, E, Auwarter, K, Luo, XD, Alonso-Alonso, M, Atassi, N, Hughes, RAC. PHASE 2 EFFICACY AND SAFETY OF RILIPRUBART, A C1S-COMPLEMENT INHIBITOR, IN CHRONIC INFLAMMATORY DEMYELINATING POLYNEUROPATHY. JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM. 2024; 29DOI:. PMID:. IF:3.200(Q2/4D).
01/08/2024
PHASE 2 TRIAL OF RILIPRUBART IN CHRONIC INFLAMMATORY DEMYELINATING POLYNEUROPATHY: QUALITY-OF-LIFE AND FATIGUE
Van Doorn, PA, Querol, L, Hartung, HP, Hughes, RAC, Orsini, M, Hakimi-Hawken, N, Minor, C, Msihid, J, Alonso-Alonso, M, Atassi, N, Lewis, R. PHASE 2 TRIAL OF RILIPRUBART IN CHRONIC INFLAMMATORY DEMYELINATING POLYNEUROPATHY: QUALITY-OF-LIFE AND FATIGUE. JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM. 2024; 29DOI:. PMID:. IF:3.200(Q2/4D).
01/08/2024
PHASE 2 TRIAL OF RILIPRUBART IN CIDP: EFFECT ON COMPLEMENT BIOMARKERS AND NEUROFILAMENT LIGHT CHAIN
Querol, L, Lewis, RA, Van Doorn, PA, Hughes, RAC, Storek, M, Rajagopal, V, Chow, T, Luo, XD, Alonso-Alonso, M, Atassi, N, Hartung, HP. PHASE 2 TRIAL OF RILIPRUBART IN CIDP: EFFECT ON COMPLEMENT BIOMARKERS AND NEUROFILAMENT LIGHT CHAIN. JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM. 2024; 29DOI:. PMID:. IF:3.200(Q2/4D).
01/08/2024
CLINICAL AND GENETIC SPECTRUM OF PATIENTS WITH BAG3-RELATED NEUROMUSCULAR DISORDERS IN EUROPE
Fernandez-Eulate, G, Gitiaux, C, Thiele, S, Jungbluth, H, Audic, F, Potulska-Chromik, A, Marini-Bettolo, C, Davion, JB, de la Tassa, GM, Olivé, M, de la Hoz, CPDF, Isapof, A, Töpf, A, Walter, M, Angelini, C, Claeys, K, Kostera-Pruszczyk, A, Attarian, S, Straub, V, Domínguez-González, C, Vissing, J, Metay, C, Khraiche, D, Wahbi, K, Stojkovic, T. CLINICAL AND GENETIC SPECTRUM OF PATIENTS WITH BAG3-RELATED NEUROMUSCULAR DISORDERS IN EUROPE. JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM. 2024; 29DOI:. PMID:. IF:3.200(Q2/4D).
01/08/2024
TREATMENT RESPONSE AND REFRACTORINESS IN PATIENTS WITH CHRONIC INFLAMMATORY DEMYELINATING POLYNEUROPATHY (INCBASE)
Michael, M, Wieske, L, Allen, J, Lunn, M, Doppler, K, Tan, CY, Koike, H, Markvardsen, L, Kapoor, M, Hsieh, ST, Nobie-Orazio, E, Jacobs, B, Rajabally, Y, Basta, I, Ripellino, P, Querol, L, Eftimov, F. TREATMENT RESPONSE AND REFRACTORINESS IN PATIENTS WITH CHRONIC INFLAMMATORY DEMYELINATING POLYNEUROPATHY (INCBASE). JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM. 2024; 29DOI:. PMID:. IF:3.200(Q2/4D).
01/08/2024
RASCH-BUILT ATAXIA RATING SALE FOR IGM-ASSOCIATED POLYNEUROPATHY WITH AND WITHOUT ANTI-MAG ANTIBODIES (IGM-PNP RB-ARS)
Hamadeh, T, van de Mortel, J, Van Doormaal, P, Cornblath, D, Vrancken, AFJE, Faber, C, Goedee, S, Minnema, M, Thomas, S, Khoshnoodi, M, Lunn, M, Keddie, S, Carr, A, D'Sa, S, Mair, D, Querol, L, Pascual-Goñi, E, Illa, CT, Harbo, T, Orazio, EN, Cutellè, C, Bianco, M, Svahn, J, Merle, H, Karlin, L, Echaniz-Laguna, A, Cauquil, C, Labeyrie, C, Peric, S, Basta, I, Palibrk, A, Stinoc, A, Briani, C, Salvalaggio, A, Marasca, M, Van den Bergh, P, Dubuisson, N, Marques, W Jr, Nascimento, O, Elsheikh, B, Doughty, C, Attarian, S, Delmont, E, Rausch, HW, Schirmer, L, Notermans, NC, Merkies, ISJ. RASCH-BUILT ATAXIA RATING SALE FOR IGM-ASSOCIATED POLYNEUROPATHY WITH AND WITHOUT ANTI-MAG ANTIBODIES (IGM-PNP RB-ARS). JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM. 2024; 29DOI:. PMID:. IF:3.200(Q2/4D).
01/08/2024
DISSECTING THE GENETIC ARCHITECTURE OF CIDP. STUDY PROTOCOL FOR AN INTERNATIONAL COLLABORATIVE GENOME-WIDE ASSOCIATION STUDY
Doneddu, P, Asselta, R, Manganelli, F, Cocito, D, Inghilleri, M, Ricciardi, D, Cavaletti, G, Di Stefano, V, Filosto, M, Carta, A, Vegezzi, E, Matà, S, Habetswallner, F, Farotti, L, Luigetti, M, Ruiu, E, Mataluni, G, Falzone, Y, Carpo, M, Leonardi, L, Gentile, L, Ripellino, P, Peric, S, Basta, I, Querol, L, Jacobs, B, Eftimov, F, Orazio, EN. DISSECTING THE GENETIC ARCHITECTURE OF CIDP. STUDY PROTOCOL FOR AN INTERNATIONAL COLLABORATIVE GENOME-WIDE ASSOCIATION STUDY. JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM. 2024; 29DOI:. PMID:. IF:3.200(Q2/4D).
01/08/2024
EFFICACY AND SAFETY OF SUBCUTANEOUS (SC) EFGARTIGIMOD PH20 IN CHRONIC INFLAMMATORY DEMYELINATING POLYNEUROPATHY: ADHERE/ADHERE plus TRIALS
Allen, J, Van Doorn, PA, Basta, I, Dysgaard, T, Eggers, C, Guptill, J, Gwathmey, K, Hewamadduma, C, Hofman, E, Hussain, Y, Kuwabara, S, Le Masson, G, Leypoldt, F, Lin, J, Lipowska, M, Lowe, M, Pinter, GL, Querol, L, Simu, MA, Chang, T, Tse, A, Ulrichts, P, Van Hoorick, B, Yamasaki, R, Lewis, RA. EFFICACY AND SAFETY OF SUBCUTANEOUS (SC) EFGARTIGIMOD PH20 IN CHRONIC INFLAMMATORY DEMYELINATING POLYNEUROPATHY: ADHERE/ADHERE plus TRIALS. JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM. 2024; 29DOI:. PMID:. IF:3.200(Q2/4D).